Status | Study |
Recruiting |
Study Name: Radiofrequency Ablation for Liver Abscesses From Chronic Granulomatous Disease Condition: Chronic Granulomatous Disease (CGD) Date: 2013-05-08 Interventions: Device: Cool-tip RF Ablation System RFA therapy will be administered according to the instructions of th |
Withdrawn |
Study Name: Lentiviral Gene Therapy for X-Linked Chronic Granulomatous Disease (X-CGD) Condition: Granulomatous Disease, Chronic, X-linked, Variant Date: 2011-06-23 Interventions: Genetic: pCCLchimGp91s lentiviral vector transduced CD34+ cells infusion pCCLchimGp91s lentiviral vector |
Recruiting |
Study Name: Targeted Busulfan, Fludarabine Conditioning Regimen for Hematopoietic Stem Cell Transplantation in Chronic Granulomatous Disease(CGD) Condition: Chronic Granulomatous Disease Date: 2011-03-04 Interventions: Drug: Busulfan First dose: busulfan (120 mg/m2 ivs once daily) (if age<1 yr: 80 mg/ m2) Second to for |
Completed |
Study Name: Gene Therapy for X-linked Chronic Granulomatous Disease (CGD) in Children Condition: Chronic Granulomatous Disease Date: 2009-06-22 Interventions: Genetic: retroviral SF71-gp91phox transduced CD34+ cells autologous ex-vivo transduced (SF71-gp91phox)CD |
Completed |
Study Name: Pharmacokinetics of Posaconazole in Children With Chronic Granulomatous Disease (CGD) Condition: Chronic Granulomatous Disease Date: 2008-11-26 Interventions: Drug: posaconazole (PSZ) Intake of PSZ oral suspension 40mg/ml twice daily with food. Starting dose is b |
Active, not recruiting |
Study Name: Gene Therapy for Chronic Granulomatous Disease in Korea Condition: Chronic Granulomatous Disease Date: 2008-10-21 Interventions: Drug: VM106 Autologous hematopoietic stem cells with MT-gp91 retroviral vector |
Recruiting |
Study Name: Matched Unrelated or Non-Genotype Identical Related Donor Transplantation For Chronic Granulomatous Disease Condition: Chronic Granulomatous Disease Date: 2007-12-19 Interventions: Drug: Busulfan |
Terminated |
Study Name: Gene Therapy for Chronic Granulomatous Disease Condition: Chronic Granulomatous Disease Date: 2007-11-26 Interventions: Drug: Phagocyte Oxidase Subunit Transduced CD34 Hematopoietic Stem Cells |
Terminated |
Study Name: Infliximab to Treat Crohn'S-like Inflammatory Bowel Disease in Chronic Granulomatous Disease Condition: Chronic Granulomatous Disease Crohn'S-like IBD Date: 2006-05-11 Interventions: Drug: Infliximab |
Completed |
Study Name: Treatment of Chronic Granulomatous Disease With Allogeneic Stem Cell Transplantation Versus Standard of Care Condition: Chronic Granulomatous Disease Date: 2001-08-29 Interventions: Drug: T-Cell Depleted & CD34+Select/w/StemCell Enriched Product |